Tuesday, June 30, 2020

How we're ending Multiple Myeloma


Our intentions are noble – put high-risk multiple myeloma patients at the forefront of our investigation to make their cure a future reality. Our process is groundbreaking – use in-house, industry-quality platforms to ensure that our breakthrough discoveries aren’t left sitting in research labs.
By combining InnovationCollaboration and Scale, the High-Risk Multiple Myeloma Moon Shot® is revolutionizing the conventional medical research approach to rapidly adapt pre-clinical findings into treatment options for high-risk multiple myeloma.orts
Overcoming poor prognosis for high-risk patients
Multiple myeloma is the second most common blood cancer and is caused by rogue plasma cells that accumulate in the bone marrow and interfere with the normal production of other blood cells. Patients with this disease can be sorted into risk groups, with high-risk symptomatic disease being characterized by significantly shortened overall survival. While treatment advances have improved clinical outcomes for patients with standard-risk symptomatic disease, high-risk multiple myeloma remains an urgent area with unmet therapeutic needs.
High-Risk Multiple Myeloma Moon Shot Leaders
·         Eric Davis, M.D. Associate Professor, Lymphoma/Myeloma
·         Elisabet Manasanch, M.D. Assistant Professor, Lymphoma/Myeloma
·         Robert Orlowski, M.D., Ph.D. Professor, Lymphoma/Myeloma and Experimental Therapeutics
Innovation
Our experts pioneered and validated a new treatment approach, which uses immune cells, called natural killer cells, to increase the effectiveness of stem cell transplantation for treatment of multiple myeloma.
Collaboration
We’re leveraging our internal and external partnerships to ensure that our investigations make a real impact. Our alliances with biotech giants such as Merck, Sanofi and Celgene to ensure our clinical trials run as smoothly and successfully as possible.
Scale
Our cellular therapy approaches are capitalizing on volume. To ensure we’re exploiting the maximum anti-tumor potential of natural killer cells, we’re increasing their numbers in the lab more than 1000 fold prior to treatment.
Help end high-risk multiple myeloma
"Even small donations, when put together, can make a huge difference and be flipped into much larger research efforts to make lives of myeloma patients better."
Listen as Moon Shot® co-leader Robert Orlowski, M.D., Ph.D., explains how your generous gift can make an impact on High-Risk Multiple Myeloma Moon Shot research projects.
Our Flagship Projects
The High-Risk Multiple Myeloma Moon Shot is focused on preventing and eradicating this disease through two treatment strategies:
1.       Immunotherapy
2.       Cellular therapy
Read more about our projects below.
PREVENTING PROGRESSION THROUGH IMMUNOTHERAPY
For patients in pre- and early-malignant disease stages, such as monoclonal gammopathy of undetermined significance (MGUS) and smoldering multiple myeloma, current guidelines recommend monitoring disease progression through watchful waiting. However, intervening earlier in the disease process may improve treatment outcomes for patients that eventually do progress to symptomatic high-risk multiple myeloma. Our Moon Shot experts are focused on improving the identification of patients at high-risk for progression and evaluating the ability for immunotherapy to delay, or prevent, progression in these patients.
ERADICATING DISEASE THROUGH CELLULAR THERAPIES
Despite treatment strategies such as high doses of chemotherapy and stem cell transplantation (SCT), patients with high-risk multiple myeloma often relapse within a year. In collaboration with the Adoptive Cell Therapy Moon Shot platform, our experts are using immune cells with powerful anti-tumor activity, called NK cells, to improve the effectiveness of SCT. Treatment using NK cells both collected from umbilical cord blood and those engineered to better target myeloma cells are being examined for their ability to improve survival outcomes for high-risk multiple myeloma patients undergoing SCT.
STORIES OF HOPE
Grateful patient gives back
Perry Rupp, of Roanoke, Texas, received a successful stem cell transplant at MD Anderson after his multiple myeloma diagnosis. He’s now giving back to the nurses who took care of him — and doing it with an eye on innovation.
RESEARCH UPDATE
Our first-in-human Phase I study examining the ability of natural killer cells to treat multiple myeloma showed promising results. The findings indicated that expanded cord blood-derived natural killer cells, combined with stem cell transplantation and high-dose chemotherapy, had little or none of the side effects seen with current treatments.
Learn more about the clinical study led by Elizabeth J. Shpall, M.D., professor of Stem Cell Transplantation and Cellular Therapy.

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